
Genethon Reports 2-Year Efficacy of Low-Dose Gene Therapy GNT0004 in Duchenne Muscular Dystrophy
Genethon Presents 2-Year Efficacy Results of Low-Dose Micro-Dystrophin Gene Therapy (GNT0004) in Duchenne Muscular Dystrophy at ESGCT 2025 Genethon, a global leader in the research and development of gene therapies for rare genetic disorders, has reported encouraging long-term results from…












