Category Press Releases

Progeria

Progeria Research Foundation and Forge Biologics Partner to Strengthen Gene Therapy Development for Children

The Progeria Research Foundation and Forge Biologics Announce Manufacturing Partnership to Advance Gene Therapy for Children with Progeria The Progeria Research Foundation (“PRF”), a nonprofit research organization dedicated to developing treatments and the cure for Hutchinson-Gilford Progeria Syndrome (“Progeria”), and…

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Kivu

Kivu Bioscience Names Brunilda Shtylla as Chief Business Officer

Kivu Bioscience Names Brunilda Shtylla as Chief Business Officer to Lead Strategic Growth and Partnership Initiatives Kivu Bioscience, a clinical-stage biotechnology company dedicated to advancing next-generation antibody-drug conjugates (ADCs) for the treatment of difficult-to-treat cancers, has announced the appointment of…

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Intellia Therapeutics Secures FDA Clearance to Resume MAGNITUDE Phase 3 Trial in ATTR-CM

Intellia Therapeutics Reports FDA Clearance to Resume MAGNITUDE Phase 3 Study in ATTR-CM Following Removal of Clinical Hold Intellia Therapeutics has cleared a significant regulatory hurdle in its effort to advance CRISPR-based gene editing into late-stage cardiovascular medicine, announcing that…

Read MoreIntellia Therapeutics Secures FDA Clearance to Resume MAGNITUDE Phase 3 Trial in ATTR-CM
FDA

FDA Accepts Takeda and Protagonist’s NDA for Rusfertide, a First-in-Class Treatment for Polycythemia Vera

Pivotal Study Shows Significant Improvements in Hematocrit Control and Patient Outcomes What does the future hold for patients with polycythemia vera (PV)? Takeda and Protagonist Therapeutics, Inc. have announced a significant milestone in the treatment of this rare blood disorder.…

Read MoreFDA Accepts Takeda and Protagonist’s NDA for Rusfertide, a First-in-Class Treatment for Polycythemia Vera
Prothena

Prothena Authorizes $100M Share Repurchase Plan to Enhance Shareholder Value

Prothena’s Strategic Move to Boost Shareholder Confidence and Financial Flexibility Why are biotechnology companies increasingly turning to share repurchase plans to optimize their financial strategies? Prothena Corporation plc, a late-stage clinical biotechnology company with a robust pipeline of investigational therapeutics,…

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Sarepta Therapeutics

Sarepta Therapeutics Launches 2026-2027 Route 79 Duchenne Scholarship Program

Sarepta Supports Educational Ambitions of Duchenne Community with $5,000 Scholarships Why is supporting the education of individuals with Duchenne muscular dystrophy crucial for the future of rare disease treatment? Sarepta Therapeutics, a leader in precision genetic medicine for rare diseases,…

Read MoreSarepta Therapeutics Launches 2026-2027 Route 79 Duchenne Scholarship Program
Evox

Evox Therapeutics Partners with RSRT to Develop Gene Editing Treatment for Rett Syndrome

Collaboration Aims to Overcome Delivery Challenges for Neurological Disorders Why has gene editing for Rett syndrome remained elusive despite its potential to reverse symptoms? Evox Therapeutics Ltd (Evox), a biotechnology company focused on developing innovative therapies for genetically driven neurodegenerative…

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